A Rare Blood Disorder, aTTP, May Start With a Simple Symptom – But

Owned by Sydney Kodatsky migraine previous attacks, but none caused sudden, complete loss of vision. This time, when Kodatsky took off his glasses after swimming, the headache intensified and the world went dark. Her husband took her to the emergency room, where they waited for more than five hours, only to be told that the …

New gene therapies could soon cure dozens of rare diseases, but

By Kevin Doxzen, Arizona State University Zolgensma – which acts spinal cord muscle atrophyA rare genetic disease that damages nerve cells and causes muscle decay, it is currently the most expensive drug in the world. One-time treatment of life-saving drug for a young child Costs 2.1 million US dollars. While the exorbitant price of Zolgensma …