New gene therapies could soon cure dozens of rare diseases, but

By Kevin Doxzen, Arizona State University Zolgensma – which acts spinal cord muscle atrophyA rare genetic disease that damages nerve cells and causes muscle decay, it is currently the most expensive drug in the world. One-time treatment of life-saving drug for a young child Costs 2.1 million US dollars. While the exorbitant price of Zolgensma …